Found 5 matching trials
Clinical Trial of Gene Therapy for Leber Congenital Amaurosis Caused by RPE65 Mutations
PHASE1The purpose of this clinical trial is to examine the safety of gene therapy...
Location
Hadassah Medical Organization
Phase 1/2 Safety and Efficacy Study of AAV-RPE65 Vector to Treat Leber Congenital Amaurosis
PHASE1The purpose of the study is to evaluate the safety and efficacy of an adeno...
Location
University of Massachusetts Medical School
Phase I Trial of Gene Vector to Patients With Retinal Disease Due to RPE65 Mutations
PHASE1A recombinant adeno-associated virus serotype 2 (rAAV2) vector has been alt...
Location
Shands Children's Hospital, University of Florida
Safety Study of RPE65 Gene Therapy to Treat Leber Congenital Amaurosis
PHASE1The purpose of the study is to determine whether gene therapy is safe and e...
Location
Moorfields Eye Hospital NHS Foundation Trust
Clinical Gene Therapy Protocol for the Treatment of Retinal Dystrophy Caused by Defects in RPE65
PHASE1The purpose of the study is to assess the safety and efficacy of the active...