Found 34 matching trials
AMX0035 in Adult Patients With Wolfram Syndrome
PHASE2This study is an open label Phase II study to evaluate the safety and effic...
Status
Active Not Recruiting
Location
Washington University
Extension Study Evaluating The Safety And Tolerability of AMX0035
PHASE3The primary objective is to evaluate the safety and tolerability of AMX0035...
Location
University Hospitals Leuven
Clinical Trial of Phenylbutyrate and Vitamin D in Tuberculosis (TB)
PHASE2Vitamin D exerts its effects via the Vitamin D Receptor (VDR) present in ac...
Location
National Institute of Diseases of Chest and Hospital (NIDCH)
To Evaluate the Safety of Long-term Use of HPN-100 in the Management of Urea Cycle Disorders (UCDs)
PHASE4This was an open-label, long-term safety study of HPN-100 (RAVICTI; glycero...
Location
UCLA Pediatrics/Genetics
Double-Blind Randomized Crossover Trial to Access Electrocardiogram Effects of HPN-100
PHASE1Arm 1:
Primary Objective:
• To determine the safety and tolerability of m...
Location
Covance Clinical Pharmacology, Inc.
Phase III Trial of AMX0035 for Amyotrophic Lateral Sclerosis Treatment
PHASE3The Phoenix Trial is a randomized double blind placebo controlled Phase III...
Status
Active Not Recruiting
Location
Barrow Neurological Institute
Glycerol Phenylbutyrate Corrector Therapy For CF (Cystic Fibrosis)
PHASE1We propose to test the effectiveness of the combination of CF pancreatic en...
Location
National Jewish Health
5-Azacytidine and Phenylbutyrate to Treat Severe Thalassemia
PHASE2This study will evaluate the safety and effectiveness of 5-azacytidine and ...
Location
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
Role of BCAA in Glucose Homeostasis
PHASE4This clinical trial study aims to evaluate the effects of prolonged NaPB tr...
Location
Multiple Locations
PBA Use for Treatment of ATF6-/- Patients
EARLY_PHASE1Some patients with achromatopsia, an inherited disorder characterized by pa...
Location
Columbia University Irving Medical Center