Found 39 matching trials
A 12-Week Safety and Pharmacodynamic Study of AT1001 (Migalastat Hydrochloride) in Participants With Fabry Disease
PHASE2Study to evaluate the safety, tolerability, and pharmacodynamics of migalas...
Location
Multiple Locations
A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding
N/AThis is a global prospective observational study of women with Fabry diseas...
Location
Amicus Therapeutics, Inc. Pregnancy Registry
A Study of Patients With Fabry Disease (US Specific)
N/AThis is an observational study to evaluate the effects of treatment on long...
Location
UAB Nephrology Research Clinic at Paula Building
Effect of Cimetidine on the Pharmacokinetics of Lucerastat in Healthy Subjects
PHASE1A study in healthy male subjects to investigate whether repeated administra...
Location
CRS Clinical Research Services Kiel GmbH
A 12-Week Safety and Pharmacodynamic Study of AT1001 (Migalastat Hydrochloride) in Female Participants With Fabry Disease
PHASE2Study to evaluate the safety, tolerability, and pharmacodynamics of migalas...
Location
Multiple Locations
Effect of Migalastat on Cardiac Involvement in Fabry Disease
N/AAnderson-Fabry Disease (AFD) is one of the rare lysosomal storage disorders...
Location
IRCCS Policlinico San Donato
A 24-Week Safety and Pharmacodynamic Study of AT1001 (Migalastat Hydrochloride) in Participants With Fabry Disease
PHASE2Study to evaluate the safety, tolerability, and pharmacodynamics of migalas...
Location
Multiple Locations
Open-Label Phase 3 Long-Term Safety Study of Migalastat
PHASE3This was a long-term, open-label study of migalastat (123 milligrams \[mg\]...
Location
Multiple Locations
A Study to Assess the Safety, Tolerability and Pharmacokinetics of Lucerastat (CDP923) After Multiple Dosing in Healthy Subjects
PHASE1The objectives of this study were to evaluate the safety and tolerability o...
Location
Investigator Site
A Study of Migalastat in Fabry Disease
N/AFabry disease is a rare metabolic condition characterised by the widespread...
Location
Manchester University Foundation Trust