Found 581 matching trials
A Prospective Study Evaluating Seroprevalence and Seroconversion of Antibodies Against Adeno-associated Virus (AAV)
NAA prospective cohort study utilizing biospecimen sample collection from adu...
Location
Instituto Hematologia Arbesu
BAY14-2222 Prophylaxis and Joint Function Improvement (Adults)
PHASE4The purpose of the study is to evaluate the effect of prophylactic treatmen...
Location
Multiple Locations
Long-term Safety and Efficacy Study of Fitusiran in Patients With Hemophilia A or B, With or Without Inhibitory Antibodies to Factor VIII or IX
PHASE3Primary Objective:
To characterize the long-term safety and tolerability o...
Status
Active Not Recruiting
Location
Phoenix Childrens Hospital Site Number : 8400009
Pharmacokinetic, Efficacy, and Safety Study of Recombinant Factor VIII Single Chain (rVIII-SingleChain) in Children With Severe Hemophilia A
PHASE3This is an international, multicenter, open-label study to assess the effic...
Comparison of Different Prophylaxis Regimens for Moderate to Severe Hemophilia A Pediatric Patients
PHASE4Title: Comparison of different prophylaxis regimens for hemophilia A pediat...
Location
Division of Hemato/oncology, Department of Pediatrics, Faculty of medicine,Chulalongkorn U
Fc factOrs and Real-World hemophiliA Patient-ReporteD Outcomes
N/AThe primary objective of the study is to evaluate the effectiveness of prop...
Medication Adherence and Non-adherence in Adults With Rare Disease
N/AThe purpose of this study is to use the Medication Adherence Reasons Scale ...
Location
Multiple Locations
Gene Therapy Study in Severe Hemophilia A Patients With Antibodies Against AAV5
PHASE1This study is being conducted by BioMarin Pharmaceutical Inc. as an open la...
Location
Charlotte Maxeke Johannesburg Academic Hospital, Hemophilia Comprehensive Care Center
The Hemophilia Inhibitor Prevention Trial
PHASE3This is a multi-center randomized phase III clinical trial, the Inhibitor P...
Location
University of Arkansas Medical Sciences Childrens Hospital
An Open Study to Investigate the Safety and Efficacy of Optivate® in Severe Haemophilia A Patients.
PHASE3The main objectives of this study are to compare the first and second recov...
Location
Klinika Haematologii, Akademia Medyczna w Bialymstokiu, ul.