Safety and Efficacy Study of Transplantation of Autologous CD34+ Cells Transduced With the G2ARTE Lentiviral Vector Expressing the DCLRE1C cDNA in Artemis (DCLRE1C) Deficient Severe Combined Immunodeficiency Patients (ARTEGENE)
PHASE1
The purpose of this study is to evaluate the Safety and Efficacy of Gene Th...
Status
Recruiting
Location
Department of Pediatric Immunology, Hematology and Rheumatology UIHR, Necker-Enfants Malades Hospital
ß-Thalassemia Major With Autologous CD34+ Hematopoietic Progenitor Cells Transduced With TNS9.3.55 a Lentiviral Vector Encoding the Normal Human ß-Globin Gene
PHASE1
The patient has inherited ß-thalassemia major through the genes. These gene...
Status
Active Not Recruiting
Location
Hospital "V.Cervello" Uoc Ematologiaii E Malattie Rare