Found 17 matching trials
A Phase 2 Study of BMN 111 to Evaluate Safety, Tolerability, and Efficacy in Children With Achondroplasia
PHASE2This is a Phase 2, open-label, sequential cohort dose-escalation study of B...
Location
Children's Hospital & Research Center Oakland
A Study of Vosoritide in Children With Noonan Syndrome With Inadequate Growth During or After Human Growth Hormone Treatment
PHASE2The purpose of this study in children with Noonan syndrome is to evaluate t...
Location
Childrens Hospital Los Angeles
A Clinical Trial to Evaluate the Safety and Efficacy of BMN 111 in Infants and Young Children With Achondroplasia
PHASE2Study 111-206 is a Phase 2 randomized, double-blind, placebo-controlled cli...
Location
Children's Hospital & Research Center Oakland
A Phase 2 Study of Vosoritide in Children With Idiopathic Short Stature
PHASE2The purpose of this study is to evaluate i) the effect of multiple doses of...
Location
Consano Clinical Research, LLC
Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia
PHASE3The purpose of this study is to evaluate the long-term safety and efficacy ...
Status
Enrolling By Invitation
Location
Nemours Children's Hospital, Delaware (Alfred I. Dupont Hospital for Children)
A Study to Evaluate Safety and Tolerability of BMN 111 Administered to Healthy Adult Volunteers
PHASE1The purpose of this study is to measure how much of the study drug gets int...
A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 Months
PHASE2The purpose of this study is to evaluate the safety and efficacy of daily a...
Location
Phoenix Children's Hospital - Thomas Campus (Main)
A Study to Evaluate Long-Term Safety, Tolerability, & Efficacy of BMN 111 in Children With Achondroplasia (ACH)
PHASE2This is a Phase 2, Open-Label, Extension Study to Evaluate the Long-Term Sa...
Status
Active Not Recruiting
Location
Children's Hospital & Research Center Oakland
An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With Achondroplasia
PHASE2This is a Phase 2, open-label multi-center long-term extension study, with ...
Status
Active Not Recruiting
Location
Children's Hospital & Research Center Oakland
An Extension Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia
PHASE3The intent and design of this Phase 3 study is to assess BMN 111 as a thera...
Status
Active Not Recruiting
Location
Children's Hospital & Research Center Oakland