Found 7 matching trials
Gene Therapy Study in Severe Hemophilia A Patients With Antibodies Against AAV5
PHASE1This study is being conducted by BioMarin Pharmaceutical Inc. as an open la...
Location
Charlotte Maxeke Johannesburg Academic Hospital, Hemophilia Comprehensive Care Center
Phase 3 Study for Efficacy and Safety Outcomes Data in Japanese Patients With Severe Hemophilia A
PHASE3This Phase III clinical study will evaluate the safety and effectiveness of...
Status
Active Not Recruiting
Location
Asahikawa Medical University Hospital
Safety, Tolerability, and Efficacy Study of Valoctocogene Roxaparvovec in Hemophilia A With Active or Prior Inhibitors
PHASE1This Phase I/II clinical study will evaluate the safety and efficacy of val...
Location
Children's Hospital Los Angeles
Study to Evaluate the Efficacy and Safety of Valoctocogene Roxaparvovec, With Prophylactic Steroids in Hemophilia A
PHASE3This Phase III clinical study will evaluate the safety and effectiveness of...
Location
University of California Davis Health
Single-Arm Study To Evaluate The Efficacy and Safety of Valoctocogene Roxaparvovec in Hemophilia A Patients at a Dose of 4E13 vg/kg
PHASE3This Phase III clinical study will assess the efficacy of BMN 270 defined a...
Location
Hemophilia Center of Western Pennsylvania
Single-Arm Study To Evaluate The Efficacy and Safety of Valoctocogene Roxaparvovec in Hemophilia A Patients (BMN 270-301)
PHASE3This Phase III clinical study will assess the impact of BMN 270 (compared t...
Location
Los Angeles Orthopedic Hospital, Orthopedic Hemophilia Treatment Center
Gene Therapy Study in Severe Haemophilia A Patients (270-201)
PHASE1This study is being conducted by BioMarin Pharmaceutical Inc. as an open la...
Location
Queen Elizabeth Hospital Birmingham