🔬 Current Disease Focus:
Task Progress: 0%
👥 Active Problem Solvers
0
🌍 Experts collaborating globally
⚡ Current Task Assignment
🧬 Genetic Analysis
🔄 Matching experts to specific tasks
📊 Resource Allocation by Research Phase:
📚 Data Analysis
🧪 Experimental Design
🔬 Clinical Trials
💊 Treatment Development
Niemann-Pick disease, type C (NPC) is a lethal, autosomal recessive, lysoso...
Status
Completed
Location
St. Louis Children's Hospital
Start Date
2019-02-22
Trial ID
NCT03471143
Treatments Being Tested
Due to different study designs, the sponsor separated Part C into a separat...
Status
Completed
Location
University of Alabama at Birmingham
Start Date
2015-10
Trial ID
NCT02534844
Treatments Being Tested
This study was amended from expanded access to a clinical trial. Informatio...
Status
Terminated
Location
University of Arkansas System
Start Date
2018-06-18
Trial ID
NCT03643562
Treatments Being Tested
Background: \- Hydroxypropyl beta cyclodextrin (HPBCD) is being tested for...
Status
Completed
Location
National Institutes of Health Clinical Center, 9000 Rockville Pike
Start Date
2013-01
Trial ID
NCT01747135
Treatments Being Tested
This is a multicenter, multinational, open-label study of VTS-270 to evalua...
Status
Terminated
Location
Hospital Clinica Biblica
Start Date
2019-12-02
Trial ID
NCT03879655
Treatments Being Tested
Due to different study designs, the sponsor separated Part C into this sepa...
Status
Terminated
Location
University of Alabama at Birmingham
Start Date
2015-12-23
Trial ID
NCT04958642
Treatments Being Tested
Background: For people who have Niemann-Pick disease, type C1 (NPC1), chol...
Status
Terminated
Location
National Institutes of Health Clinical Center
Start Date
2020-01-06
Trial ID
NCT03887533
Treatments Being Tested
This is a Phase-2, multicenter, multiple dose, open-label, 2-part evaluatio...
Status
Withdrawn
Location
Multiple Locations
Start Date
2020-05
Trial ID
NCT03687476
Treatments Being Tested