Found 17 matching trials
A Study of UX007 (Triheptanoin) in Participants With Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD)
PHASE2The primary objective of the study was to evaluate the impact of UX007 on a...
Location
Children's National Medical Center
Anaplerotic Therapy Using Triheptanoin for Patients With Glycogen Storage Disease Type I
EARLY_PHASE1This study will be an open-label, prospective, interventional feasibility p...
Location
Duke University Medical Center
Triheptanoin (UX007) to Treat Citrate Transporter Deficiency
N/AThe purpose of this study is to determine whether triheptanoin (UX007) is e...
Status
No Longer Available
Location
Department of Neurology, Boston Children's Hospital
Treatment of Mitochondrial Dysfunction in Rett Syndrome With Triheptanoin
PHASE2The aim of this study is to evaluate the safety and tolerability of trihept...
Location
Center for Rare Neurological Diseases
Study to Assess the Long Term Safety and Efficacy of UX007 in Participants With Glucose Type 1 Deficiency Syndrome (Glut1 DS)
PHASE2The primary objective of the study is to evaluate the long-term safety of U...
Location
Children's Hospital Colorado - University of Colorado, Denver, School of Medicine
A Study to Determine the Effect of Triheptanoin Compared With Even-Chain MCT on MCEs in Pediatric Patients With LC-FAOD
PHASE3The main goal of this study is to evaluate the effects of triheptanoin vers...
Status
Active Not Recruiting
Location
General University Hospital in Prague-GUH (Všeobecná fakultní nemocnice v Praze- VFN)
Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program
N/AThe primary objective of this study is to assess the long-term safety, incl...
Status
Active Not Recruiting
Location
Phoenix Children's Hospital
Open Label Trial of Triheptanoin (UX007) in Treatment of Rett Syndrome.
PHASE2This is a single-center, exploratory, open-label study in 10 girls diagnose...
Location
Multiple Locations
Phase 2 Study of Triheptanoin (UX007) for the Treatment of Glucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)
PHASE2The primary objectives of the study are to evaluate the efficacy of UX007 c...
Location
Children's Hospital Colorado - University of Colorado, Denver, School of Medicine
Treatment With UX007 for a Single Patient With GLUT1 Deficiency Syndrome
N/AThis treatment plan is intended for the use of UX007 (triheptanoin) in the ...
Status
No Longer Available
Location
Children's Hospital of Pittsburgh of UPMC