🔬 Current Disease Focus:
Task Progress: 0%
👥 Active Problem Solvers
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🌍 Experts collaborating globally
⚡ Current Task Assignment
🧬 Genetic Analysis
🔄 Matching experts to specific tasks
📊 Resource Allocation by Research Phase:
📚 Data Analysis
🧪 Experimental Design
🔬 Clinical Trials
💊 Treatment Development
Individual patient expanded access requests may be considered for patients ...
Status
Available
Location
Multiple Locations
Start Date
TBD
Trial ID
NCT03775174
Treatments Being Tested
Emergency access granted to treat a single patient with advanced Mucopolysa...
Status
No Longer Available
Location
Cohen Children's Medical Center
Start Date
TBD
Trial ID
NCT02097251
Treatments Being Tested
UX003-CL201 is an open-label Phase 1/2 study to assess the safety, efficacy...
Status
Completed
Location
Manchester Academic Health Science Centre
Start Date
2013-11
Trial ID
NCT01856218
Treatments Being Tested
The primary objective of the study is to evaluate the long-term safety of U...
Status
Completed
Location
Children's Hospital Oakland
Start Date
2015-11-10
Trial ID
NCT02432144
Treatments Being Tested
The Phase 3 study will use a novel randomized, intra-subject placebo-contro...
Status
Completed
Location
Children's Hospital Oakland
Start Date
2014-12
Trial ID
NCT02230566
The objectives of this study are to characterize MPS VII disease presentati...
Status
Recruiting
Location
Children's Hospital of Orange County
Start Date
2018-01-29
Trial ID
NCT03604835
Treatments Being Tested
The primary objective was to evaluate the effect of UX003 treatment in pedi...
Status
Completed
Location
Children's National Health System
Start Date
2015-07-21
Trial ID
NCT02418455
Treatments Being Tested