Found 40 matching trials
Treatment Development of Triheptanoin (G1D)
PHASE1To determine the maximum tolerated dose (MTD), as a percentage of calories ...
Location
UT Southwestern Medical Center
Triheptanoin Treatment Trial for Patients With Adult Polyglucosan Body Disease
PHASE2The purpose of the study is to determine if triheptanoin is an effective tr...
Location
Department of Genetics, Groupe Hospitalier Pitié-Salpêtrière
Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) Deficiency
PHASE1This is a medical research study to test a medication in patients with a di...
Location
UPMC Children's Hospital of Pittsburgh
A Study of UX007 (Triheptanoin) in Participants With Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD)
PHASE2The primary objective of the study was to evaluate the impact of UX007 on a...
Location
Children's National Medical Center
Anaplerotic Therapy Using Triheptanoin for Patients With Glycogen Storage Disease Type I
EARLY_PHASE1This study will be an open-label, prospective, interventional feasibility p...
Location
Duke University Medical Center
Triheptanoin (UX007) to Treat Citrate Transporter Deficiency
N/AThe purpose of this study is to determine whether triheptanoin (UX007) is e...
Status
No Longer Available
Location
Department of Neurology, Boston Children's Hospital
Phase II Open Label Study Using Triheptanoin in Patients With Glucose Type 1 Transporter Deficiency GLUT1-DS
PHASE2The purpose of this project is to study the efficacy of triheptanoin oil in...
Location
Brain and Spine Institute
Study of Triheptanoin for Treatment of Long-Chain Fatty Acid Oxidation Disorder
PHASE2Humans eat long-chain fat in their diet and use it for energy during exerci...
Location
Oregon Health & Science University
Treatment of Mitochondrial Dysfunction in Rett Syndrome With Triheptanoin
PHASE2The aim of this study is to evaluate the safety and tolerability of trihept...
Location
Center for Rare Neurological Diseases
Ataxia-telangiectasia: Treating Mitochondrial Dysfunction With a Novel Form of Anaplerosis
PHASE2Study design: Parallel group, placebo-controlled, dose-escalation each 2 mo...
Location
Queensland Children's Hospital