Found 5 matching trials
Retroviral Insertion Site Methodology Study
PHASE4Adenosine deaminase (ADA) is an enzyme involved in the development and func...
Location
Multiple Locations
Evaluating the Effectiveness of STRIMVELIS Risk Minimization Measures (RMMs)
N/ASTRIMVELIS is a medicinal product that restores adenosine deaminase (ADA) f...
Location
Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET)
ADA Gene Transfer Into Hematopoietic Stem/Progenitor Cells for the Treatment of ADA-SCID
PHASE2This is a phase I/II protocol to evaluate the safety and efficacy of ADA ge...
Location
Investigational Site
Strimvelis Registry Study to Follow-up Patients With Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID)
N/AAdenosine deaminase (ADA) enzyme deficiency results in severe combined immu...
Status
Enrolling By Invitation
Location
Ospedale San Raffaele
Methodology Study of Retroviral Insertion Site Analysis in Strimvelis Gene Therapy
N/AThis study is a post approval commitment to evaluate the accuracy and preci...
Location
Ospedale San Raffaele