Found 5 matching trials
A Study of PTC923 (CNSA-001) in Primary Tetrahydrobiopterin (BH4) Deficient Participants With Hyperphenylalaninemia
PHASE1This study has been designed to demonstrate the safety, pharmacokinetics (P...
Location
University of Minnesota
A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria
PHASE3The main purpose of this study is to evaluate the long-term safety of PTC92...
Status
Active Not Recruiting
Location
Children's Hospital Colorado
Impact Of A Phe-Restricted Diet On Gut Health In Children With PKU
N/APhenylketonuria (PKU) is an inherited disorder of phenylalanine (Phe) metab...
Location
Birmingham Children's Hospital
A Study of CNSA-001 in Women With Diabetic Gastroparesis
PHASE2This study evaluates CNSA-001 (sepiapterin) in the treatment of women with ...
Location
GW Research, Inc.
A Study of Sepiapterin in Participants With Phenylketonuria (PKU)
PHASE3The main purpose of this trial is to evaluate the long-term efficacy of sep...
Location
Indiana University School of Medicine