Found 5 matching trials
An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy PHASE3 The main objective of this study is to evaluate the safety and tolerability...
Show More Location
Neuromuscular Research Center
Learn More & Join Trial
Study of SRP-4045 (Casimersen) and SRP-4053 (Golodirsen) in Participants With Duchenne Muscular Dystrophy (DMD) PHASE3 The main objective of this study is to evaluate the efficacy of SRP-4045 (c...
Show More Location
Neuromuscular Research Center
Learn More & Join Trial
A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice N/A This is a phase 4, multicenter, prospective, observational study designed t...
Show More Status
Enrolling By Invitation
Location
Arkansas Children's Hospital Research Institute
Learn More & Join Trial
A 48-Week, Open Label, Study to Evaluate the Efficacy and Safety of AMONDYS 45, EXONDYS 51, VYONDYS 53 in Subjects With DuchenneMuscular Dystrophy Carrying Eligible DMD Duplications. PHASE2 This is an 48-week open-label study to determine the efficacy and safety of...
Show More Location
Nationwide Children's Hospital
Learn More & Join Trial
Phase I/II Study of SRP-4053 in DMD Patients PHASE1 This is a first-in-human, multiple-dose 2-part study to assess the safety, ...
Show More Location
Boston Children's Hospital
Learn More & Join Trial