Found 4 matching trials
Gene Therapy for Fanconi Anemia, Complementation Group A
PHASE2The objective of this study is to assess the therapeutic efficacy of a hema...
Status
Active Not Recruiting
Location
Stanford University
Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A
PHASE2This is an open-label Phase II clinical trial to evaluate the efficacy of a...
Location
Hospital Infantil Universitario Niño Jesús (HIUNJ)
Long-Term Follow-up: Phase I/II Clinical Study to Evaluate the Safety and Efficacy of the Infusion of RP-L102
N/ALong-Term Follow-up: Phase I/II clinical study to evaluate the safety and e...
Status
Enrolling By Invitation
Location
Lucille Packard Children's Hospital, Stanford University
A Clinical Trial to Evaluate the Safety of RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A
PHASE1The objective of this study is to assess the therapeutic safety and prelimi...
Location
Stanford University Institute for Stem Cell Biology and Regenerative Medicine Lucille Packard Children's Hospital, Stanford University