Found 24 matching trials
A Study of Safety and Efficacy of HPN-100 in Subjects With Cirrhosis and Episodic Hepatic Encephalopathy
PHASE2This is a phase 2 study of HPN-100 in subjects with hepatic encephalopathy ...
Location
Stanford University Medical Center, Division of Gastroenterology and Hepatology
To Evaluate the Safety of Long-term Use of HPN-100 in the Management of Urea Cycle Disorders (UCDs)
PHASE4This was an open-label, long-term safety study of HPN-100 (RAVICTI; glycero...
Location
UCLA Pediatrics/Genetics
Double-Blind Randomized Crossover Trial to Access Electrocardiogram Effects of HPN-100
PHASE1Arm 1:
Primary Objective:
• To determine the safety and tolerability of m...
Location
Covance Clinical Pharmacology, Inc.
Glycerol Phenylbutyrate Corrector Therapy For CF (Cystic Fibrosis)
PHASE1We propose to test the effectiveness of the combination of CF pancreatic en...
Location
National Jewish Health
Expanded Access Protocol for an Intermediate Size Population - RAVICTI for Byler Disease
N/AByler Disease is the result of a homozygous missense (G308V) mutation in th...
Status
No Longer Available
Location
Multiple Locations
PBA Use for Treatment of ATF6-/- Patients
EARLY_PHASE1Some patients with achromatopsia, an inherited disorder characterized by pa...
Location
Columbia University Irving Medical Center
Study of Glycerol Phenylbutyrate & Sodium Phenylbutyrate in Phenylbutyrate Naïve Patients With Urea Cycle Disorders (UCDs)
PHASE4This is a randomized, controlled, open-label parallel arm study to assess t...
Location
University of Florida (UF) - Shands Hospital
Use of Ravicti™ in Patients With MCAD Deficiency With the 985A>G (K304E) Mutation
PHASE1This is a medical research study to test a medication in adult patients wit...
Location
Children's Hospital of Pittsburgh of UPMC
Observational Study That Will Collect Information on Patients With Urea Cycle Disorders (UCDs)
N/ATHRIVE is an observational study that will collect information on patients ...
Location
United BioSource Corporation
Dose-Escalation Safety Study of HPN-100 to Treat Urea Cycle Disorders
PHASE2The purpose of this study is to determine whether HPN-100 is safe and toler...
Location
University of Minnesota