Found 4 matching trials
A Study of PTC923 (CNSA-001) in Primary Tetrahydrobiopterin (BH4) Deficient Participants With Hyperphenylalaninemia
PHASE1This study has been designed to demonstrate the safety, pharmacokinetics (P...
Location
University of Minnesota
A Study of PTC923 in Participants With Phenylketonuria
PHASE3The main purpose of this trial is to evaluate the efficacy of PTC923 in red...
Location
Stanford University Center for Academic Medicine
A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria
PHASE3The main purpose of this study is to evaluate the long-term safety of PTC92...
Status
Active Not Recruiting
Location
Children's Hospital Colorado
A Study of Sepiapterin in Participants With Phenylketonuria (PKU)
PHASE3The main purpose of this trial is to evaluate the long-term efficacy of sep...
Location
Indiana University School of Medicine