Found 12 matching trials
Sapropterin in Individuals With Phenylketonuria
N/AInvestigators at Washington University will examine the effects of sapropte...
Location
Washington University
The Effects of Kuvan on Functional Brain Connectivity in Individuals With Phenylketonuria (PKU)
N/AThe objective of the study is to determine whether Kuvan™ (sapropterin) imp...
Location
University of Missouri
A 16 Week Study Evaluating the Introduction of a GMP Based Protein Substitute in Participants With PKU
NAThis study aims to measure changes in participants' blood phenylalanine (Ph...
Location
Kreiskliniken Reutlingen
PKU Protein Requirements
NAThe objective of this research is to determine the protein requirements bas...
Location
Emory University Hospital
Behavioral Effects of Kuvan in Children With Mild Phenylketonuria
N/AThe purpose of this study is to determine whether improvements in behavior ...
Location
Northwestern University/Children's Memorial Hospital
Acceptability and Tolerance of a Ready-to-use Protein Substitute in Tablet Form for the Dietary Management of Phenylketonuria
N/AThe purpose of this prospective, observational study is to evaluate the tol...
Location
Birmingham Children´s Hospital
PKUDOS: Phenylketonuria (PKU) Demographic, Outcomes, and Safety Registry
N/AThe objective of this study is to evaluate the safety of long-term treatmen...
Location
Childrens Hospital of Los Angeles
Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With Phenylketonuria
PHASE3This is a Phase 3 open-label randomized controlled study enrolling approxim...
Status
Active Not Recruiting
Location
Phoenix Children's Hospital
A Clinical Study on the Safety and Tolerability of PL54 Injection in Adult Patients With Phenylketonuria (PKU)
PHASE1The primary objective of this clinical trial is to evaluate the safety and ...
Location
The First Affiliated Hospital of Anhui Medical University
Safety and Efficacy of Self Administered Injections of Pegvaliase (>40mg/Day Dose) in Adults With PKU
PHASE3This is a Phase 3 open-label extension study enrolling adult patients with ...
Location
University of Florida