Found 0 matching trials
Arginine and Buphenyl in Patients With Argininosuccinic Aciduria (ASA), a Urea Cycle Disorder
PHASE2Urea cycle disorders are inherited illnesses in which the body does not pro...
Location
Baylor College of Medicine
Immune Reconstitution in Tuberculosis Disease
PHASE2The aim with study is to provide adjunctive therapy with vitamin D and phen...
Location
Black Lion Hospital (BLH), Addis Ababa University, Faculty of Medicine
PBA Use for Treatment of ATF6-/- Patients
EARLY_PHASE1Some patients with achromatopsia, an inherited disorder characterized by pa...
Location
Columbia University Irving Medical Center
AMX0035 in Patients With Amyotrophic Lateral Sclerosis (ALS)
PHASE2The CENTAUR trial was a 2:1 (active:placebo) randomized, double-blind, plac...
Location
Barrow Neurological Institute
Safety, Tolerability and Effectiveness of Nuedexta in the Treatment of Pseudobulbar Affect (PBA)
PHASE4The objectives of the study are to evaluate the safety, tolerability, and e...
Location
Multiple Locations
A Healthy Volunteer Study to Compare Fezagepras (PBI-4050) With Sodium Phenylbutyrate
PHASE1The purpose of this study is to compare the safety, tolerability and pharma...
Azacitidine Plus Phenylbutyrate in Treating Patients With Acute Myeloid Leukemia or Myelodysplastic Syndrome
PHASE1RATIONALE: Azacitidine plus phenylbutyrate may help leukemia cells develop ...
Location
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
Study of Glycerol Phenylbutyrate & Sodium Phenylbutyrate in Phenylbutyrate Naïve Patients With Urea Cycle Disorders (UCDs)
PHASE4This is a randomized, controlled, open-label parallel arm study to assess t...
Location
University of Florida (UF) - Shands Hospital
Phenylbutyrate in Proteinuric Nephropathies
PHASE2The purpose of this study is to determine whether sodium phenylbutyrate can...
Location
Hôpital Necker Enfants Malades
Use of Ravicti™ in Patients With MCAD Deficiency With the 985A>G (K304E) Mutation
PHASE1This is a medical research study to test a medication in adult patients wit...
Location
Children's Hospital of Pittsburgh of UPMC