🔬 Current Disease Focus:
Task Progress: 0%
👥 Active Problem Solvers
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🌍 Experts collaborating globally
⚡ Current Task Assignment
🧬 Genetic Analysis
🔄 Matching experts to specific tasks
📊 Resource Allocation by Research Phase:
📚 Data Analysis
🧪 Experimental Design
🔬 Clinical Trials
💊 Treatment Development
To evaluate the safety, tolerability and efficacy of intravenous administra...
Status
Completed
Location
Novartis Investigative Site
Start Date
2021-09-08
Trial ID
NCT04851873
Treatments Being Tested
This was a Phase III multi-center, single dose (1.2 x 10\^14 vector genomes...
Status
Completed
Location
Connecticut Children's Medical Center
Start Date
2022-02-01
Trial ID
NCT05089656
Treatments Being Tested
This was a phase IV Open-label, single-arm, single-dose, multicenter study,...
Status
Completed
Location
Novartis Investigative Site
Start Date
2021-11-04
Trial ID
NCT05073133
Treatments Being Tested
Phase 3, open-label, single-arm, single-dose, trial of onasemnogene abeparv...
Status
Completed
Location
University Hospital Ghent Neuromuscular reference center
Start Date
2018-08-16
Trial ID
NCT03461289
Treatments Being Tested
This is a global, prospective, multi-center study that is designed to asses...
Status
Active Not Recruiting
Location
Child Hosp Of The Kings Daughters
Start Date
2022-12-19
Trial ID
NCT05335876
Treatments Being Tested
This was a Phase IIIb open-label, single arm, multi-center study to evaluat...
Status
Completed
Location
Boston Childrens Hospital
Start Date
2023-01-12
Trial ID
NCT05386680
Treatments Being Tested