Found 385 matching trials
Long-term Safety and Efficacy Study of Fitusiran in Patients With Hemophilia A or B, With or Without Inhibitory Antibodies to Factor VIII or IX
PHASE3Primary Objective:
To characterize the long-term safety and tolerability o...
Status
Active Not Recruiting
Location
Phoenix Childrens Hospital Site Number : 8400009
Pharmacokinetic, Efficacy, and Safety Study of Recombinant Factor VIII Single Chain (rVIII-SingleChain) in Children With Severe Hemophilia A
PHASE3This is an international, multicenter, open-label study to assess the effic...
Comparison of Different Prophylaxis Regimens for Moderate to Severe Hemophilia A Pediatric Patients
PHASE4Title: Comparison of different prophylaxis regimens for hemophilia A pediat...
Location
Division of Hemato/oncology, Department of Pediatrics, Faculty of medicine,Chulalongkorn U
Fc factOrs and Real-World hemophiliA Patient-ReporteD Outcomes
N/AThe primary objective of the study is to evaluate the effectiveness of prop...
Gene Therapy Study in Severe Hemophilia A Patients With Antibodies Against AAV5
PHASE1This study is being conducted by BioMarin Pharmaceutical Inc. as an open la...
Location
Charlotte Maxeke Johannesburg Academic Hospital, Hemophilia Comprehensive Care Center
The Hemophilia Inhibitor Prevention Trial
PHASE3This is a multi-center randomized phase III clinical trial, the Inhibitor P...
Location
University of Arkansas Medical Sciences Childrens Hospital
An Open Study to Investigate the Safety and Efficacy of Optivate® in Severe Haemophilia A Patients.
PHASE3The main objectives of this study are to compare the first and second recov...
Location
Klinika Haematologii, Akademia Medyczna w Bialymstokiu, ul.
China ADVATE PTP Study
PHASE4The purpose of this study is to assess efficacy, safety and pharmacokinetic...
Location
Peking Union Medical College Hospital
Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis
N/AHemophilia A (HA) is a genetic bleeding disorder resulting from a deficienc...
Location
Arkansas Children's Hospital
Register of Patients With haEmophilia A tReated With Afstyla®
N/ARecord real life data of patients with Hemophilia A and treated with Afstyl...