Found 28 matching trials
Feasibility, Validation and Application of Digital Tools for the Follow-up of Neuromuscular Patient Mobility in Daily Living
NAThe low prevalence of rare diseases hinders the design of clinical studies ...
Location
Association Institut de Myologie
Romiplostim in Combination With CsA vs. CsA in the Treatment of Newly Diagnosed NSAA
PHASE4Aplastic anemia (AA) is a group of clinical syndromes caused by a significa...
Location
Peking union medical college hospital
A Prospective Study on the Treatment of Recurrent/Refractory/Intolerable NSAA With Lusutrombopag
PHASE4In a prospective, single-arm study, the efficacy and safety of Lusutrombopa...
Location
Peking Union Medical College Hospital
Efficacy of IST Combined With TPO-RA in the Treatment of AA and Establishment of a Recurrence Prediction System
PHASE4In this study, investigators intend to prospectively study treatment-naive ...
Location
Peking union medical college hospital
NSAA NON-Interventional Study Protocol
N/AThe purpose of this non-interventional study is to evaluate the feasibility...
Location
Red Nucleus Solutions
A Study of Romiplostim for the Treatment of Refractory Transfusion-dependent NSAA
PHASE4Efficacy and safety of Romiplostim in the treatment of refractory transfusi...
Location
Peking Union Medical College Hospital
CsA+EPAG/HPAG+Romiplostim N01 in the Treatment of Newly-diagnosed SAA/TD-NSAA
PHASE2This study aimed to explore the efficacy and safety of cyclosporine (CsA) c...
Location
Multiple Locations
Enzalutamide in First Line Androgen Deprivation Therapy for Metastatic Prostate Cancer
PHASE3The purpose of this study is to determine the effectiveness of enzalutamide...
Status
Active Not Recruiting
Location
Dana Farber Cancer Institute
CsA+EPAG/HPAG+Romiplostim N01 in Newly-diagnosed SAA/TD-NSAA
PHASE2This study aimed to explore the efficacy and safety of cyclosporine (CsA)
...
Location
Multiple Locations
Natural History Study for Patients With Nemaline Myopathy in Spain
N/AThe objective of this natural history study is to comprehensively character...
Location
University Hospital Vall d'Hebron