Found 0 matching trials
Characterization of New Phenotypes of Patients With Spinal Muscular Atrophy Treated With SMN Restoring Therapy
NAWith the advent of new treatments for ASI, new phenotypes are emerging. The...
Location
Pediatric Rehabilitation Service - L'Escale Mother and Child Hospital
A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
PHASE2This double-blind, Phase 2, multiple-dose study will be conducted to evalua...
Location
Phoenix Children's Hospital
Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies
PHASE3This is a Phase 3, open-label, single-arm, single-dose, trial of onasemnoge...
Location
Tokyo Women's Medical University
Skeletal Muscle Atrophy and Dysfunction Following Total Knee Arthroplasty
NATotal knee replacement, or arthroplasty, is the final clinical intervention...
Location
University of Vermont College of Medicine
Outpatient Rehabilitation Intervention for Young Children With SMA
NAAn outpatient rehabilitation program for children (6 months to less than 6 ...
Location
Holland Bloorview Kids Rehabilitation Hospital
Efficacy of a Semi-occluded Mask in the Treatment of Patients With Voice Disorders
NACurrent semi-occluded vocal tract therapies limit the type of vocalizations...
Location
University of Pittsburgh
Transforming Growth Factor Beta Signalling in the Development of Muscle Weakness in Pulmonary Arterial Hypertension
N/APulmonary arterial hypertension (PAH) is a disease that causes raised blood...
Location
Royal Brompton Hospital
Exploratory Study of Respiratory Bacterial Infections or Superinfections and Colonizations in Patients With Spinal Muscular Atrophy Under NIV
NASMA (Spinal Muscular Atrophy) is a rare neuromuscular disease characterized...
Location
Centre Hospitalier Universitaire d'Amiens
Muscle Stimulation for Physical Function During Stem Cell Transplant
NASome blood, bone marrow, and lymphatic (hematologic) cancers such as Hodgki...
Location
VA Puget Sound Health Care System Seattle Division, Seattle, WA
Peripheral Neurofilament Levels and Amyotrophic Lateral Sclerosis
N/ATo evaluate the correlation between peripheral neurofilament levels and cli...
Location
Peking University Third Hospital