Found 0 matching trials
Kuvan®'s Effect on the Cognition of Children With Phenylketonuria
PHASE4The study is a single-cohort, interventional, open-label trial to evaluate ...
Study on Sapropterin Dihydrochloride Oral Suspension in Healthy Subjects Under Fed Conditions
PHASE1This is a single center, Phase 1, randomized, open-label, single-dose, 2 tr...
Location
Pharma Medica Research Inc. 4770 Sheppard Ave E,
Retrospective Observational Safety Effectiveness With Kuvan in hpA
N/AA retrospective study to collect the effectiveness and safety data of the p...
Location
West China Hospital of Sichuan University
Sapropterin on Cognitive Abilities in Young Adults With Phenylketonuria
PHASE2This is a Phase 2a multicenter, double-blind, placebo-controlled, randomize...
Study on Sapropterin Dihydrochloride Oral Suspension in Healthy Subjects
PHASE1This is a single center, Phase 1, randomized, open-label, single-dose, 4 tr...
Location
Pharma Medica Research Inc. 4770 Sheppard Ave E,
Cystic Fibrosis and Endothelial Function: At Rest and During Exercise
PHASE2Perhaps one of the most disturbing aspects of Cystic Fibrosis (CF) is the a...
Location
Georgia Prevention Institute/ Laboratory of Integrative and Exercise Physiology
A Single Patient Study of Sapropterin for Multisystem Smooth Muscle Dysfunction Syndrome
NAThere is currently no approved treatment for multisystem smooth muscle dysf...
Location
CHU Sainte-Justine
Phenylketonuria, Oxidative Stress, and BH4
PHASE2The purpose of this study is to see how tetrahydrobiopterin therapy (BH4; a...
Open-Label Extension Study of Kuvan for Autism
PHASE2This is an open-label extension study available only to subjects who comple...
Location
The Children's Health Council
Long Term Nitric Oxide Bioavailability on Vascular Health in Chronic Obstructive Pulmonary Disease
PHASE2Chronic obstructive pulmonary disease (COPD) affects up to 14 million peopl...
Location
Georgia Prevention Institute