A Safety and Dose Ranging Study of Idursulfase (Intrathecal) Administration Via an Intrathecal Drug Delivery Device in Pediatric Patients With Hunter Syndrome Who Have Central Nervous System Involvement and Are Receiving Treatment With Elaprase®
PHASE1
Elaprase (idursulfase), a large molecular protein, is not expected to cross...
Study of Intrathecal Idursulfase-IT Administered in Conjunction With Elaprase® in Pediatric Patients With Hunter Syndrome and Early Cognitive Impairment
PHASE2
Study HGT-HIT-094 is a multicenter study designed to determine the effect o...
Status
Completed
Location
Children's Hospital and Research Center at Oakland
An Extension Study of HGT-HIT-045 Evaluating Long-Term Safety and Clinical Outcomes of Idursulfase-IT in Conjunction With Elaprase in Pediatric Participants With Hunter Syndrome and Cognitive Impairment
PHASE1
This extension study of HGT-HIT-045 is designed to collect long-term safety...
Status
Completed
Location
Ann & Robert H Lurie Childrens Hospital of Chicago