🔬 Current Disease Focus:
Task Progress: 0%
👥 Active Problem Solvers
0
🌍 Experts collaborating globally
⚡ Current Task Assignment
🧬 Genetic Analysis
🔄 Matching experts to specific tasks
📊 Resource Allocation by Research Phase:
📚 Data Analysis
🧪 Experimental Design
🔬 Clinical Trials
💊 Treatment Development
Primary Objective: To characterize the long-term safety and tolerability o...
Status
Active Not Recruiting
Location
Phoenix Childrens Hospital Site Number : 8400009
Start Date
2019-01-09
Trial ID
NCT03754790
Treatments Being Tested
This is a multicenter, multinational, open-label, one-way cross-over, Phase...
Status
Active Not Recruiting
Location
Center for Inherited Blood Disorders (CIBD) Site Number : 8400012
Start Date
2023-02-01
Trial ID
NCT05662319
Primary Objective: To characterize the frequency of bleeding episodes (BE)...
Status
Completed
Location
Investigational Site Number 0139
Start Date
2018-07-25
Trial ID
NCT03549871
Treatments Being Tested
Primary Objective: -To evaluate the efficacy of fitusiran compared to on-d...
Status
Completed
Location
Investigational Site Number 0140
Start Date
2018-03-01
Trial ID
NCT03417245
Treatments Being Tested
This is an exploratory, single group, Phase 4, study to assess treatment wi...
Status
Recruiting
Location
Children's Hospital Los Angeles- Site Number : 8400005
Start Date
2024-03-01
Trial ID
NCT06145373
Primary Objective: \- To confirm appropriate dose levels of fitusiran when...
Status
Active Not Recruiting
Location
Children's Hospital Los Angeles Site Number : 8400002
Start Date
2020-01-28
Trial ID
NCT03974113
Treatments Being Tested
Primary Objective: To evaluate the long-term safety and tolerability of fi...
Status
Completed
Location
Clinical Trial Site
Start Date
2015-09-18
Trial ID
NCT02554773
Treatments Being Tested
The purpose of this study was to determine the frequency of bleeding episod...
Status
Completed
Location
Investigational Site Number 0117
Start Date
2018-02-14
Trial ID
NCT03417102
Treatments Being Tested
This is a parallel, Phase 3, two-arm, open-label study to evaluate the effi...
Status
Recruiting
Location
The Luskin Orthopaedic Institute for Children- Site Number : 8400013
Start Date
2025-12-18
Trial ID
NCT07285460