🔬 Current Disease Focus:
Task Progress: 0%
👥 Active Problem Solvers
0
🌍 Experts collaborating globally
⚡ Current Task Assignment
🧬 Genetic Analysis
🔄 Matching experts to specific tasks
📊 Resource Allocation by Research Phase:
📚 Data Analysis
🧪 Experimental Design
🔬 Clinical Trials
💊 Treatment Development
The purpose of this extension study is to evaluate the ongoing safety and t...
Status
Terminated
Location
UZ-Gent
Start Date
2019-06-26
Trial ID
NCT03985878
Treatments Being Tested
This is an open-label study to assess the safety, tolerability, efficacy an...
Status
Completed
Location
Neuromuscular Research Center of Arizona
Start Date
2015-06-30
Trial ID
NCT02420379
Treatments Being Tested
Part 1 (dose escalation) will evaluate the safety and tolerability of 2 dos...
Status
Active Not Recruiting
Location
University of Alabama at Birmingham
Start Date
2020-07-13
Trial ID
NCT03992430
Treatments Being Tested
This is an 48-week open-label study to determine the efficacy and safety of...
Status
Completed
Location
Nationwide Children's Hospital
Start Date
2020-02-18
Trial ID
NCT04179409
Treatments Being Tested
The primary objective of this study is to assess the ongoing efficacy, safe...
Status
Completed
Location
Miller Children's Hospital
Start Date
2012-02-27
Trial ID
NCT01540409
Treatments Being Tested
The primary objective of this study is to explore safety and tolerability o...
Status
Completed
Location
Ronald Reagan UCLA Medical Center
Start Date
2014-11
Trial ID
NCT02286947
Treatments Being Tested
The main objective of this study is to provide evidence of efficacy of etep...
Status
Completed
Location
Neuromuscular Research Center
Start Date
2014-11-17
Trial ID
NCT02255552
Treatments Being Tested
This is a multicenter, open-label, dose-escalation study to evaluate the sa...
Status
Completed
Location
Universitair ziekenhuis Gent
Start Date
2017-08-16
Trial ID
NCT03218995
Treatments Being Tested
The specific aim of this Phase I/II study is to assess the safety of intrav...
Status
Completed
Location
Great Ormond Street Hospital
Start Date
2009-01
Trial ID
NCT00844597
Treatments Being Tested
This is a phase 4, multicenter, prospective, observational study designed t...
Status
Enrolling By Invitation
Location
Arkansas Children's Hospital Research Institute
Start Date
2019-01-07
Trial ID
NCT06606340
Treatments Being Tested