Found 21 matching trials
Vatiquinone Expanded Access Protocol
N/AThe purpose of this study is to provide participants who successfully compl...
Status
No Longer Available
Location
Multiple Locations
EPI-743 in Friedreich's Ataxia Point Mutations
PHASE2The purpose of this study is to evaluate the effects of EPI-743 in patients...
Location
University of South Florida
Safety and Efficacy Study of EPI-743 in Children With Leigh Syndrome
PHASE2The purpose of this study is to evaluate the effects of EPI-743 in children...
Location
Stanford University
A Study of Vatiquinone for the Treatment of Participants With Friedreich Ataxia
PHASE2The primary objective of the study is to assess the pharmacokinetics (PK) a...
Location
The Children's Hospital of Philadelphia
Long-Term Safety and Efficacy Evaluation of EPI-743 in Children With Leigh Syndrome
PHASE2EPI-743 in Leigh syndrome participants that participated in previous EPI743...
A Study to Evaluate Efficacy and Safety of Vatiquinone for Treating Mitochondrial Disease in Participants With Refractory Epilepsy
PHASE2This is a parallel-arm, double-blind, placebo-controlled study with a scree...
Location
University of California
Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA)
PHASE3The purpose of this study is to confirm the treatment effects of vatiquinon...
Location
University of California Los Angeles
Safety and Efficacy of EPI-743 in Patients With Friedreich's Ataxia
PHASE2The purpose of this study is to examine the effects of EPI-743 on visual fu...
Location
University of California Los Angeles
EPI-743 for Metabolism or Mitochondrial Disorders
PHASE1Background:
* Mitochondria are the parts of cells that help produce energy...
Location
National Institutes of Health Clinical Center, 9000 Rockville Pike
Emergency Administration of EPI-743 to a Single Patient With Leber's Hereditary Optic Neuropathy [LHON]
N/AExpanded access Protocol to treat LHON subjects with EPI743...
Status
No Longer Available
Location
Doheny Eye Institute / UCLA