Found 71 matching trials
Study of Velaglucerase Alfa Enzyme Replacement Therapy in Japanese Patients With Gaucher Disease
PHASE3Gaucher disease is an inherited deficiency of the lysosomal enzyme glucocer...
Location
Hamamatsu University School of Medicine
A Study of the Tolerability, Safety, and Pharmacokinetics of ISU302 in Healthy Volunteers
PHASE1The purpose of this study is to assess the safety, tolerability, and pharma...
Location
Multiple Locations
Long Term Impact of Rapid Intravenous Infusion of Velaglucerase Alfa (VPRIV)
PHASE4Background: In order to allow our satisfied patients, who have successfully...
Location
Multiple Locations
Biomarker Analysis for GBA Associated Parkinson's Disease
N/AThe primary aim of the study is to conclusively demonstrate the possibility...
Study to Evaluate the Efficacy and Safety of Venglustat in Adult and Pediatric Patients With Gaucher Disease Type 3
PHASE3This is a parallel arm, Phase 3, double-blind, double-dummy, active-compara...
Status
Active Not Recruiting
Location
Yale University School of Medicine - Investigational Site Number: 8400003
Genotypic Influences on Network Progression in Parkinson's Disease
N/AIn this longitudinal study, the investigators will follow Parkinson's disea...
Status
Active Not Recruiting
Location
Feinstein Institutes for Medical Research
A Switch-Over Study of the Safety and Efficacy of ISU302 in Patients With Type 1 Gaucher Disease
N/AThe purpose of this study is to evaluate the safety and efficacy of ISU302 ...
Location
Multiple Locations
Lentiviral Vector Gene Therapy - The Guard1 Trial of AVR-RD-02 for Subjects With Type 1 Gaucher Disease
PHASE1This was a multinational, open-label study to assess the safety and efficac...
Location
University of California San Diego
A Multicenter Extension Study of Taliglucerase Alfa in Pediatric Subjects With Gaucher Disease
PHASE3A protocol to extend the assessment of the safety and efficacy of taligluce...
Location
Shaare Zedek Medical Center
A Study of the Efficacy and Safety of Eliglustat Tartrate (Genz-112638) in Type 1 Gaucher Patients
PHASE2Gaucher disease is a genetic disease that results in a deficiency of an enz...
Location
New York University