Found 9 matching trials
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
N/ATo obtain short-term and long-term clinical safety information, in pediatri...
Location
Children's National Hospital
Orphan Europe Carbaglu® Surveillance Protocol
N/AThe purpose of this study is to conduct post-marketing surveillance of carg...
Location
Children's National Medical Center
Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia
PHASE3A Phase IIIb (Three b), Randomized Multicentre Comparative Trial to Evaluat...
Location
King Abdullah Specialist Children Hospital, King Abdulaziz Medical City
Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia
PHASE2The overall objective of this drug trial is to determine whether the treatm...
Location
University of California Los Angeles
Long-term Efficacy of Carglumic Acid in Organic Acidemia.
NAEvaluate the Long Term Effectiveness \& Safety of the use of Carglumic Acid...
Location
National Taiwan University Hospital
N-Carbamylglutamate (Carbaglu) In The Treatment Of Hyperammonemia
PHASE2This study is based on the hypothesis that a new drug N-carbamylglutamate (...
Location
Childrens Research Institute
Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia
PHASE2Background: Very few drugs exist that treat hyperammonemia, specifically PA...
Location
University of California Los Angeles
Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate
PHASE2Hyperammonemia, which can cause brain damage, occurs in many different kind...
Location
Multiple Locations
Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach
N/AThis is a prospective mixed-design study focused on the long-term managemen...
Location
Hopital Des Enfants, CHU de Bordeaux-GH Pellegrin