Found 15 matching trials
Safety and Tolerability of VGB-R04 in Patients With Haemophilia B
EARLY_PHASE1An Open-Label, Non-Randomized, uncontrolled, single-dose pilot study of VGB...
Location
Blood diseases hospital
A Gene Therapy Study for Hemophilia B
PHASE2A Phase 1/2, Open-Label, Non-Randomized, Dose-Escalation Study of SPK-9001 ...
Location
UC Davis Comprehensive Cancer Center
The Efficacy and Safety of ZS801 in Chinese Hemophilia B Patients.
NAA non-randomized, open-label study to evaluate the safety, kinetics and eff...
Location
Institute of Hematology & Blood Diseases Hospital
HOPE-B: Trial of AMT-061 in Severe or Moderately Severe Hemophilia B Patients
PHASE3This is an open-label, single-dose, multi-center, multinational trial to de...
Location
Phoenix Children's Hospital
A Study to Evaluate the Safety and Efficacy of ZS801 in Adult Hemophilia B Patients
PHASE1A non-randomized, open-label, dose-escalation, phase I/II study to evaluate...
Location
Institute of Hematology & Blood Diseases Hospital
Gene Therapy for Hemophilia B Patients Aged 12-18 Years Old
PHASE1This is a Phase 1, open- label, non- randomized, uncontrolled, single dose ...
Location
Institute of haematology and Blood diseases hospital
Phase 1/2 Dose Confirmation Study of FLT180a in Hemophilia B
PHASE1Study of FLT180a gene therapy in adults with Hemophilia B. Up to 9 patients...
Location
Children's Hospital of Los Angeles
Safety of a New Type of Treatment Called Gene Transfer for the Treatment of Severe Hemophilia B
PHASE1In this study a modified virus called adeno-associated virus (AAV) will be ...
Location
Stanford University
Long-term Safety and Efficacy Study and Dose-Escalation Substudy of PF 06838435 in Individuals With Hemophilia B
PHASE2Long-term safety and efficacy follow-up for participants with Hemophilia B ...
Location
UC Davis Comprehensive Cancer Center
Trial of AAV5-hFIX in Severe or Moderately Severe Hemophilia B
PHASE1This study evaluates how safe gene therapy treatment with AAV5-hFIX is in a...
Location
uniQure Investigative Site