Found 4 matching trials
Lentiviral Vector Gene Therapy - The Guard1 Trial of AVR-RD-02 for Subjects With Type 1 Gaucher Disease
PHASE1This was a multinational, open-label study to assess the safety and efficac...
Location
University of California San Diego
A Long-Term Follow-up Study of Subjects With Gaucher Disease Who Previously Received AVR-RD-02
N/AThis is a multicenter, multinational long-term follow-up study to assess th...
Location
University of Iowa
An Efficacy and Safety Study of AVR-RD-02 Compared to Enzyme Replacement Therapy for Treatment of Gaucher Disease Type 3
PHASE2The purpose of this study is to evaluate the efficacy and safety of autolog...
Location
Multiple Locations
Long Term Follow-Up for Safety of AVR-RD-02
N/AThe goal of this observational study is to assess the safety and tolerabili...
Status
Active Not Recruiting
Location
University of Iowa Hospitals and Clinics